Published on 31.08.2026
Presentation
Team
Scientific Publications
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2022Journal (source)Nat MedLong-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: t...
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Journal (source)Mol Ther Methods Clin DevSuccessful Preclinical Development of Gene Therapy for Recombinase-Activating...
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2020Journal (source)BloodClonal tracking in gene therapy patients reveals a diversity of human hematop...
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2019Journal (source)HaematologicaExtensive multilineage analysis in patients with mixed chimerism after alloge...
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2019Journal (source)Bone Marrow TransplantEx vivo generated human T-lymphoid progenitors as a tool to accelerate immune...
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2016Journal (source)Stem Cells Dev.Gene Therapy with Hematopoietic Stem Cells: The Diseased Bone Marrow's Point ...
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2014Journal (source)J Allergy Clin ImmunolSuccessful RAG1-SCID gene therapy depends on the level of RAG1 expression.
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2014Journal (source)J Allergy Clin ImmunolThe BLNK adaptor protein has a nonredundant role in human B-cell differentiat...
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2013Journal (source)J Allergy Clin ImmunolRecombination-activating gene 1 (Rag1)-deficient mice with severe combined im...